NHP National Voxelotor Guideline
In January 2022 Voxelotor was given a positive Scientific opinion for the Early Access to Medicine Scheme (EAMS), which programme allows for promising new unlicensed medicines to be used outside their licence, to UK patients that have a high unmet clinical need.
The guideline for use has been published by the National Haemoglobinopathy Panel working group.
Access the document here.