New Therapies
With the advent of much new research and emerging therapies, we seem to be in a golden age in haemoglobinopathy treatment.
Stay tuned as we share highlights of this exciting journey
Treatments
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Crizanlizumab
This first-in-class monoclonal antibody is use to reduce frequency in vast-occlusive episodes and is currently being used under a managed access programme (MAA).
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Voxelotor
This novel drug is indicated for the treatment of haemolytic anaemia in adult and paediatric patients with Sickle Cell Disease.